Table 1 Patient characteristics
From: Severe combined immunodeficiency: improved survival leading to detection of underlying liver disease
Number of patients in the cohort (n) | 18 |
|---|---|
Median age (years) | 11.5(3.5–30.0) |
Males [n (%)] | 11 (61%) |
BMI percentile (median) | 75.5 |
Race [n(%)] | |
White | 10 (55%) |
African-American | 5 (27%) |
Native American | 1 (5%) |
Multiracial | 1 (5%) |
Unknown | 1 (5%) |
Gene Therapy [n(%)] | 7 (38%) |
HSCT [n(%)] | 5 (27%) |
ERT [n(%)] | 18 (100%) |